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PI3K inhibition in combination with tamoxifen in patients with metastatic HR+/HER2- breast cancer: clinical and circulating tumor DNA results - PubMed

3 months ago
  • #PI3K inhibitor
  • #breast cancer
  • #ctDNA
  • Study evaluates taselisib (PI3K inhibitor) combined with tamoxifen in metastatic HR+/HER2- breast cancer patients.
  • POSEIDON trial: Phase II, randomized, placebo-controlled, conducted from 2016 to 2020.
  • Primary endpoint: Progression-free survival (PFS) improvement with taselisib + tamoxifen vs. placebo + tamoxifen (4.8 vs. 3.2 months).
  • Significant toxicity noted with taselisib, including diarrhea (40% any grade).
  • Exploratory ctDNA analysis links high tumor fraction at baseline to worse PFS and OS.
  • Conclusion: Efficacy shown but tolerability concerns limit clinical benefit; ctDNA may aid patient selection.