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Dysregulation of astrocytic DNAJC6 contributes to sporadic Parkinson's disease pathogenesis - PubMed

6 hours ago
  • #Parkinson's Disease
  • #DNAJC6
  • #Astrocytes
  • DNAJC6 mutations cause juvenile-onset familial Parkinson's disease (PD).
  • DNAJC6 expression is downregulated in sporadic PD brains and stem cell models.
  • Downregulation involves transcriptional factors NURR1/FOXA2 and LRRK2-mediated stability.
  • DNAJC6 is also expressed in astrocytes and reduced in sporadic PD.
  • Loss in astrocytes impairs cellular functions and increases inflammation, worsening neurodegeneration.
  • Restoring DNAJC6 via CRISPRa in a PD mouse model improved symptoms and pathology.
  • Targeting DNAJC6 in neurons and astrocytes may be a therapeutic strategy for sporadic PD.