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Genetic Drivers of Sensitivity or Resistance to RAS(ON) Multi-Selective Inhibitors in NRAS-Mutated Melanoma - PubMed

4 hours ago
  • #NRAS melanoma
  • #RAS inhibitors
  • #Drug resistance
  • RAS(ON) multi-selective inhibitors like RMC-7977 and daraxonrasib show potent anti-proliferative activity against NRAS-mutated melanoma.
  • Resistance to RMC-7977 monotherapy in preclinical models arises via mutations in Ppia (CYPA) or Map2k1 (MEK1).
  • Daraxonrasib demonstrated anti-tumor activity in one NRAS-mutated melanoma patient, but progressive disease in another with co-occurring NRAS and MAP2K1 mutations.
  • The findings support daraxonrasib's potential for treating NRAS-mutated melanoma and highlight monotherapy resistance mechanisms.
  • Combination therapies may be needed to improve outcomes for patients with NRAS-mutated melanoma.