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Human CSF proteogenomics links genetic variation to neurodegenerative disease proteins - PubMed

5 hours ago
  • #GWAS
  • #neurodegenerative diseases
  • #proteogenomics
  • Largest single-site CSF genome-wide association study (GWAS) analyzed 7,092 SomaScan proteins in 1,259 individuals.
  • Identified 1,971 genome-wide significant pQTLs (954 cis, 971 trans), with 1,409 replicating in an independent CSF dataset.
  • Discovered 264 new loci, replicated 511 associations, refined 80 known loci, and identified 265 proxy-based associations.
  • Robust discovery concentrated in reliable measurements, highlighting the need for rigorous quality control.
  • Enrichment analyses revealed immune/complement and extracellular matrix biology.
  • Mendelian randomization prioritized causal proteins for neurodegenerative diseases like Alzheimer's, Parkinson's, Creutzfeldt Jacobs disease, and ALS.