New gene therapy slows progression of Huntington's disease by 75%
a day ago
- #gene therapy
- #Huntington's disease
- #medical breakthrough
- New gene therapy AMT-130 slows Huntington's disease progression by 75%.
- Delivered via brain surgery, a single dose is expected to last a lifetime.
- Principal investigator Professor Ed Wild calls the results 'world-changing'.
- Trial participants showed significant stability, with some able to return to work.
- Potential to preserve daily function and delay symptom onset in early-stage patients.
- Findings bring hope to the Huntington's disease community and may impact other neurodegenerative disorders.