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Efficacy of Pyridostigmine in Myasthenia Gravis: A Randomized, Double-Blind, Placebo-Controlled Crossover Trial - PubMed

6 hours ago
  • #Myasthenia Gravis
  • #Randomized Trial
  • #Pyridostigmine
  • Pyridostigmine significantly improved Myasthenia Gravis symptoms (MGII score difference: 5.3) in a randomized trial.
  • Secondary measures (QMG, MG-ADL, MG-QOL15r) also showed significant benefits for pyridostigmine over placebo.
  • Cost-utility analysis indicated lower annual costs (€6,565) and improved quality-adjusted life years (0.106 QALYs) with pyridostigmine.
  • The study provides Class I evidence for pyridostigmine's efficacy in anti-acetylcholine receptor-positive myasthenia gravis.