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Efficacy and safety of mufemilast in patients with Behçet's syndrome: a phase 2 randomised clinical trial - PubMed

4 hours ago
  • #PDE4 inhibitor
  • #Behçet's syndrome
  • #clinical trial
  • Study evaluated mufemilast, a PDE4 inhibitor, in Behçet's syndrome patients with active oral ulcers.
  • Randomized trial with 90 patients assigned to mufemilast (45 mg, 60 mg) or placebo for 12 weeks.
  • Primary endpoint: AUC for oral ulcers from baseline to week 12.
  • Mufemilast significantly reduced oral ulcers and improved pain scores vs. placebo (P < .001).
  • Safety profile was acceptable with transient PDE4-related side effects and low discontinuation rates.
  • No serious adverse events related to mufemilast were reported.