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The NPR1 agonist antibody XXB750 in heart failure: a phase 2 randomized trial - PubMed

7 hours ago
  • #NPR1 agonist
  • #clinical trial
  • #heart failure
  • XXB750, a human monoclonal antibody targeting natriuretic peptide receptor 1 (NPR1), was evaluated in a phase 2 randomized trial for heart failure with reduced ejection fraction.
  • Patients were randomized to receive 60 mg XXB750, 120 mg XXB750, placebo, or open-label sacubitril/valsartan, with NT-proBNP change at 16 weeks as the primary endpoint.
  • Contrary to expectations, XXB750 increased NT-proBNP levels and decreased cGMP levels, while sacubitril/valsartan decreased NT-proBNP and increased cGMP.
  • XXB750 was associated with more frequent death or worsening heart failure events (25%) compared to sacubitril/valsartan (8%) and placebo (0%), leading to premature trial termination.
  • The results suggest XXB750 may paradoxically act as a functional antagonist of endogenous natriuretic peptides in heart failure patients.