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Dystrophins DP71 and DP427 determine cell viability during proliferation and myofibre differentiation - PubMed

3 hours ago
  • #Duchenne muscular dystrophy
  • #cell viability
  • #dystrophin isoforms
  • DP71 and DP427 dystrophins are key for cell viability during proliferation and myofiber differentiation, respectively, affecting disease severity in DMD.
  • Absence of DP71 or DP427 leads to similar cellular defects like increased membrane permeability and ROS, but triggers distinct transcriptome changes impacting proliferation vs. structural reorganization.
  • Utrophin UP395 can partially compensate for both DP427 and DP71, influencing therapeutic strategies for DMD patients with different dystrophin deficiencies.