Treatment-related benefit and satisfaction in patients with Fabry disease in France: insight into patients' expectations and preferences from the prospective, non-interventional SATIS-Fab study - PubM
10 days ago
- #Patient benefit
- #Fabry disease
- #Treatment satisfaction
- SATIS-Fab研究评估了法国法布里病患者在两年内的治疗相关获益和满意度。
- 大多数患者处方了米加司他，通过患者获益指数（PBI）报告了稳定较高的治疗获益。
- 从酶替代疗法（ERT）转为米加司他显著提高了治疗获益和满意度评分。